“In your hearts honor Christ, the Lord as holy, always being prepared to make a defense to anyone who asks you for a reason for the hope that is in you; yet do it with gentleness and respect.” (1 Peter 3:15 ESV )
I had the opportunity recently to travel to Washington DC to attend an FDA advisory committee meeting. Over 800 parents, children and family members were in attendance that day showing support for approval of "Eteplirsen”, the first ever drug to treat Duchenne Muscular Dystrophy.
As you can imagine, emotions were high as we spent the morning and early afternoon listening to doctors and researchers presenting their charts and graphs showing the outcome of the clinical trial. We all were hoping there would be enough evidence to convince the committee that this drug was worthy of their approval..... click on link below to continue reading...
